Type 1 spinal muscular atrophy (SMA), also called infantile-onset SMA or Werdnig-Hoffmann disease, is the most common form of SMA, accounting for about 60% of cases. SMA is a rare genetic disease ...
Itvisma is the first gene replacement therapy approved for a broad SMA population, including adolescents, teens, and adults with SMN1 mutations. Phase III STEER and Phase IIIb STRENGTH trials showed ...
SMA Solar Technology AG (ETR:S92), is not the largest company out there, but it led the XTRA gainers with a relatively large price hike in the past couple of weeks. Shareholders may appreciate the ...
Private credit fintech Percent has launched SMAs focused on private credit investments. The SMAs will invest in asset-backed loans valued at under $25 million, with the firm providing deal selection, ...
The 34th Seoul Music Awards (SMA) has unveiled its third lineup! On May 26, the 34th Seoul Music Awards revealed its third lineup of artists including NCT’s Doyoung, NCT WISH, ILLIT, ZEROBASEONE, ...
Spinal muscular atrophy (SMA) is an autosomal recessive neuromuscular disease caused by deletions or mutations in the Survival Motor Neuron 1 gene, associated with high morbidity and mortality related ...
Cybersecurity company SonicWall has warned customers that two older vulnerabilities impacting its Secure Mobile Access (SMA) appliances are now being actively exploited in attacks. On Tuesday, ...
A pair of clinical data sets gives Novartis confidence in a new formulation of the company’s gene therapy Zolgensma for the treatment of older patients with spinal muscular atrophy (SMA). Among SMA ...
Moving averages are technical analysis indicators designed to smooth out price movements by determining an average price over a period of time. There are two major types of moving averages in use – ...
More than three years after Novartis’ plan for a speedy approval for intrathecal Zolgensma was thwarted by an FDA requirement for a pivotal phase 3 trial, the company is back with a positive readout ...
A phase 3 trial of Biohaven’s taldefgrobep alfa in spinal muscular atrophy (SMA) has missed its primary endpoint. The biotech plans to talk to the FDA about the next steps in SMA and is stepping up ...
Superior mesenteric artery (SMA) syndrome is a condition that affects the duodenum — the section of the small intestine that joins the stomach. The syndrome is caused by the compressing of the ...