Roche is hoping to undercut hugely expensive rivals after the FDA approved its oral spinal muscular atrophy (SMA) drug Evrysdi (risdiplam). Evrysdi is the third treatment approved for SMA, an ...

Roche and PTC Therapeutics' Evrysdi for spinal muscular atrophy (SMA) has been approved by the FDA for younger children with the rare disease, extending its use to include infants less than two months ...

A five-year-old boy who received the world's most expensive drug as a baby has made "incredible progress" and can walk independently, his mother said. Edward, from Colchester, has spinal muscular ...

Edward was one of the first children in England to be given the gene therapy Zolgensma through the NHS A five-year-old boy who received the world's most expensive drug as a baby has made "incredible ...

Several programs and personalities of GMA Network earned recognition at the Anak TV Seal Awards 2025. According to Bernadette Reyes' report on "24 Oras" on Tuesday, GMA Network's flagship newscast "24 ...

Unified managed accounts (UMAs) and separately managed accounts (SMAs) are two account types that offer high-net-worth clients more control and flexibility than mutual funds. Both options let you ...

Despite possessing a solid data package on the potential of high-dose Sprinraza in spinal muscular atrophy (SMA), Biogen will now need to revise its application if it hopes to secure an FDA nod. The ...

SMA Solar Technology AG said its Sunny Central Storage battery inverter has become the first system in Germany to receive a unit certificate for grid-forming mode with instantaneous reserve. The ...

The Create Energy and SMA Solar teams at SMA’s German headquarters. The partnership will see SMA Solar restart US manufacturing after a decade-long absence. Image: SMA Solar German inverter ...

SMA type 3 is a hereditary disease that affects motor neurons. People may also refer to it as Kugelberg-Welander disease. Symptoms usually begin after 18 months of age. Children with SMA type 3 can ...

Risdiplam, an oral pre–messenger RNA splicing modifier, is an efficacious treatment for persons with symptomatic spinal muscular atrophy (SMA). The safety and efficacy of risdiplam in presymptomatic ...

PICTURES OUT FRONT. NEW AT FIVE FLORIDA FACES A MAJOR SHORTAGE OF PSYCHIATRISTS, RANKING AMONG THE WORST STATES IN THE NATION. BUT ONE FLORIDA CENTRAL FLORIDA BEHAVIORAL HEALTH CARE PROVIDER HOPES TO ...